Hope for Marian

Global Genes Global Advocacy Alliance member focused on rare disease support, education, advocacy, or research. A medical research charitable foundation intent on advancing drug development, research, education and patient access to care for Niemann-Pick Type C (NPC). NPC is a fatal and neurodegenerative storage disorder also called “Childhood Alzheimer’s,” impacting hundreds to thousands of children and adults around the world. Directory information only; not medical advice, legal advice, or endorsement. Services and eligibility should be confirmed with the organization.