Rare Trait Hope Fund

The mission and primary exepmt purpose is to facilitate research, raise funds and support development of treatments for Aspartylglucosaminuria (AGU); to be the resource for doctors, scientists and families world-wide; to increase awareness of rare diseases in general and Aspartylglucosaminuria in particular.

Per FDA feedback from pre-IND meeting in 2018, gene therapy product production is complete. It will be used in a clinical trial for AGU treatment.

AGA drug product vector safety and toxicology study per task order 1, agreement #AGR00026049 signed October 17, 2022.

Rare Trait Hope Fund is a 501(c)(3) nonprofit (EIN 46-2762646) based in Belle Chasse, LA.